The family of a boy with a severe degenerative muscle disease has urged their local hospital to prescribe a drug that could help slow down the progress of the condition. Six-year-old Jack was ...

Muscular dystrophy is a disease caused by mutations in the dystrophin gene. The muscles of muscular dystrophy patients weaken and atrophy over time. Heart and breathing muscles may also eventually be ...

12-year-old Deklan Locke, who has Duchenne muscular dystrophy, uses a power wheelchair and raises awareness about the disease. Duchenne muscular dystrophy is a rare genetic disorder that causes muscle ...

Sarepta’s blockbuster gene therapy has come under scrutiny following a string of patient deaths.

Riley Moser is a digital producer who covers breaking news and feature stories for CBS Minnesota. Riley started her career at CBS Minnesota in June 2022 and earned an honorable mention for sports ...

This story is republished from STAT, the health and medicine news site that’s a partner to the Globe. Sign up for STAT’s free Morning Rounds newsletter here. Wave Life Sciences’ experimental treatment ...